"My medicine is making me stronger," 7-year-old Hudson Sanford says after receiving a breakthrough gene therapy for Duchenne Muscular Dystrophy Cara Lynn Shultz is a writer-reporter at PEOPLE. Her ...

A patient has died following treatment with Elevidys, the Sarepta Therapeutics product that is the only FDA-approved gene therapy for Duchenne muscular dystrophy, the company disclosed Tuesday. The ...

Davia Jones said it took seven years for her son, Kyrie, to be diagnosed with Duchenne Muscular Dystrophy, a progressive ...

Sarepta stock popped Wednesday after the company reported promising results for its gene-silencing tech in two forms of muscular dystrophy.

A LAYTOWN family is racing against time to raise €2.7 million for life-changing treatment in the United States for their ...

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

From Philly and the Pa. suburbs to South Jersey and Delaware, what would you like WHYY News to cover? Let us know! Yuva Gambhir has a full life. The University of Pennsylvania senior studies cognitive ...

Disorders like muscular dystrophies are difficult to treat using gene therapies because of a size problem. The dysfunctional genes in these conditions are often very big, and current methods used in ...

BRAINERD — Motorcycle riders and enthusiasts from across the world will soon descend on Brainerd as they work to raise awareness and fight Duchenne muscular dystrophy. Hosted by Brainerd's Craig ...

A charity transforms a garden in Brierley Hill for two brothers with Duchenne Muscular Dystrophy.

Capricor has reapplied for FDA approval of deramiocel, its therapy for DMD-related heart disease, and expects a decision by ...