On April 28, 2026 the Jeffrey Modell Foundation (JMF) will host Luigi D. Notarangelo, M.D., the Chief of the Immune Deficiency Genetics Section at the National Institute of Allergy and Infectious ...
Upon approval, Rocket has been awarded a priority review voucher, which currently fetch around $200m on the secondary market.
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FDA OKs therapy for deadly pediatric immune disorder
Kids with severe LAD-I, caused by ITGB2 mutations, are at risk of life-threatenin ...
The FDA has approved Kresladi, the first gene therapy for severe Leukocyte Adhesion Deficiency Type I. Designed for pediatric ...
Dr. Donald Kohn has been developing gene therapies for rare pediatric immune disorders for over 30 years. This week, his role in a clinical trial has culminated in the first-ever U.S. Food and Drug ...
If approved, Joenja® (leniolisib) would become the first approved treatment in the European Union for activated phosphoinositide 3-kinase delta ...
The influenza virus or flu is a contagious respiratory illness that can generate mild, moderate, or severe symptoms. Healthy individuals that contract the virus may feel mild symptoms, but recover ...
Primary immunodeficiency (PI) is a group of more than 400 disorders that affect the immune system. In people with PI, the immune system is weakened or missing important components, making it harder ...
Specific antibody deficiency (SAD) is an immune system disorder. It occurs when you have normal levels of antibodies but an insufficient immune response to certain types of bacteria. Antibodies, also ...
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