Learn how gene editing is transforming sickle cell disease treatment and why expanding access to younger children matters.
Elijah Dottery spent months at a time at a children’s hospital in Ann Arbor battling sickle cell anemia and its complications ...
Gene editing has delivered remarkable results against sickle cell disease. Now researchers are working to make these ...
Sickle cell anemia causes sickle-shaped cells to block blood flow to the lungs, leading to acute chest syndrome. Common treatment methods involve oxygen supplementation and pain management. Sickle ...
The first person to ever be cured of sickle cell anemia in Louisiana received revolutionary gene therapy. The treatment is ...
People with sickle cell anemia, especially children, are more likely to experience a stroke. Silent strokes, which don’t cause noticeable symptoms, are especially common. Sickle cell anemia (SCA) is a ...
Elijah Dottery spent months at a time at a children’s hospital in Ann Arbor battling sickle cell anemia and its complications ...
Children with sickle cell anemia are vulnerable to serious infections and stroke, but many do not receive the preventative care that could help them stay healthier for longer, a Children's Hospital ...
Exa-cel, a new CRISPR-based treatment, modifies the genes of the patient's stem cells to induce them to produce fetal hemoglobin. I have a long-standing interest in sickle cell anemia, a genetic ...
The Sickle Cell Anemia Testing and Screening Market offers growth opportunities through expanded newborn testing, molecular ...
FDA’s PDUFA goal date is November 1, 2026If approved, mitapivat is positioned to become the first oral PK activator for patients with sickle cell ...