Patients with sickle cell disease and beta-thalassemia treated with exagamglogene autotemcel reported substantial and ...

Agios Pharmaceuticals, Inc. (Nasdaq: AGIO), a commercial-stage biopharmaceutical company focused on delivering innovative medicines for patients with rare diseases, today announced that the Committee ...

PYRUKYND is currently approved in Europe for adults with PK deficiency; thalassemia would represent its second indication, ...

Agios Pharmaceuticals said a key European regulatory committee has recommended expanded approval of its Pyrukynd anemia drug for certain people with the inherited blood disorder thalassemia. Agios on ...

In 2024, regulators approved Casgevy, the first CRISPR-based therapy to treat sickle cell disease and beta-thalassemia — a ...

A South Memphis woman is tying pink and purple together in honor of Breast Cancer Awareness Month and Domestic Violence Month ...

Jaipur: A study by doctors at the govt-run JK Lon Hospital has found that nearly 43% of children with thalassemia who undergo ...

Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with the Italian Medicines Agency (AIFA) for eligible transfusion-dependent beta thalassemia (TDT) and severe sickle ...

A South Memphis woman is tying pink and purple together in honor of Breast Cancer Awareness Month and Domestic Violence Month ...

Three-year-old Meher from Noida was diagnosed with Turner Syndrome at PGICH using QF-PCR, a first for the institute. Early ...

The Human Genome Project, launched in 1990 and completed in 2003, also moved the needle. Scientists had successfully ...

The median annual net price of drugs launched from 2022 to 2024 increased by 51%, according to a new analysis from the ...