Agios Pharmaceuticals, Inc. (Nasdaq: AGIO), a commercial-stage biopharmaceutical company focused on delivering innovative medicines for patients with rare diseases, today announced that the Committee ...

PYRUKYND is currently approved in Europe for adults with PK deficiency; thalassemia would represent its second indication, ...

Vertex Pharmaceuticals Incorporated remains a leader in CF treatments, fueling robust cash flow and pipeline expansions.

Agios Pharmaceuticals said a key European regulatory committee has recommended expanded approval of its Pyrukynd anemia drug for certain people with the inherited blood disorder thalassemia. Agios on ...

Sanofi (SNY) stock and Insmed (INSM) stock are in focus as new treatments from the companies win backing from an expert panel ...

We expect Vertex Pharmaceuticals VRTX to surpass expectations when it reports its third-quarter 2025 results on Nov. 3, after market close. The Zacks Consensus Estimate for the to-be-reported ...

Bristol-Myers Squibb Company (($BMY)) announced an update on their ongoing clinical study. Study Overview: Bristol-Myers ...

Patients with sickle cell disease and beta-thalassemia treated with exagamglogene autotemcel reported substantial and ...

Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with the Italian Medicines Agency (AIFA) for eligible transfusion-dependent beta thalassemia (TDT) and severe sickle ...

System76 Pop!_OS 24.04 beta is now available. COSMIC desktop is an out-of-this-world environment. You can download and install the beta now for free. Over 10 years ...

GameSpot may get a commission from retail offers. Early access for the Call of Duty: Black Ops 7 beta starts today, and Treyarch has released some new patch notes regarding changes and new additions ...

The Call of Duty: Black Ops 7 Open Beta gives players a first look at the game before its official release on November 14 The Call of Duty: Black Ops 7 Open Beta gives players a first look at the game ...