Cell and gene therapy company ENCell said on the 6th that its allogeneic umbilical cord-derived mesenchymal stem cell therapy candidate "EN001" received orphan drug designation (ODD) from the U.S.

A WORD must really be said against the recent revival of what may be called the Cult of Muscle. This cult of muscle, or belief in physical culture, so called, as the true means of race-culture, ...

A gene therapy for Duchenne muscular dystrophy caused complications to the liver, prompting a review of its use for younger patients. By Christina Jewett The Food and Drug Administration said on ...

New interim data from a Phase III trial puts the company on track to file for FDA approval next year in an indication that not only lacks a disease-modifying treatment but suffered significant ...

We collaborate with the world's leading lawyers to deliver news tailored for you. Sign Up for any (or all) of our 25+ Newsletters. Some states have laws and ethical rules regarding solicitation and ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

Sarepta Therapeutics’ report of a second fatality this year in a patient dosed with its Duchenne muscular dystrophy gene therapy raised the prospect it might have to pull the product from the market.

PARIS, June 28 2025—The Heads of Multilateral Development Banks (MDBs) met today in Paris, hosted by the Council of Europe Development Bank (CEB), which currently chairs the Heads of MDBs Group. The ...

The Finance Committee of the Portland City Council today advanced a policy that would exempt new residential projects from system development charges for a three-year period beginning 30 days after ...

OR POOLS. STARTING TOMORROW, IOWANS WILL BE ABLE TO FILE FOR UNEMPLOYMENT AND SEARCH FOR JOBS ALL IN ONE LOCATION. IT’S PART OF A NEW UNEMPLOYMENT SYSTEM. THE STATE IS LAUNCHING. IOWA WORKFORCE ...