The latest understandings in SMA disease type, severity, and progression. Plus, how to make an accurate diagnosis and ...
After 5 years on oral treatment Evrysdi, 90% of children with SMA type 1 were alive, and many reached motor milestones, a ...
Muscle ultrasound helps assess muscle health and its association with motor function in SMA children treated with Spinraza, a ...
The one-time gene therapy Itvisma will now be available for people with SMA of all ages in the European Union after winning ...
A study found Evrysdi (risdiplam) helps the body produce more SMN, and also revealed genetic differences between SMA types 2 and 3.
For guest writer Maria Llave, having consistent access to Medicaid provides peace of mind, enabling her to focus on her future.
Columnist Kevin Schaefer says that the days of having a hospital room as a place of residency are hopefully behind him, which ...
While attending concerts, columnist Connie Chandler was frustrated that she was unable to express joy. Then she found a clap ...
Columnist Brianna Albers says that moving out of her long-time home with SMA has turned out to be her biggest gamble yet.
Weak bones in SMA may be due to impaired muscle-to-bone communication. This disruption could be tied to the SNAP23 protein. Restoring SNAP23 or replenishing these vesicles shows promise for improving ...